Panelists discuss how recent advancements in muscular dystrophy treatment have evolved toward truly disease-modifying therapies using gene replacement, antisense oligonucleotides, and gene transfer ...

Experts discuss the landscape of treatment options for Duchenne muscular dystrophy, examine the benefits and risks of gene therapy and conventional steroid treatments, and emphasize the need for early ...

A research team led by Associate Professor Hidetoshi Sakurai and Researcher Nana Takenaka-Ninagawa recently demonstrated the superior therapeutic potential of iPS cell-derived mesenchymal stromal ...

A new gene therapy treatment for Duchenne muscular dystrophy (DMD) shows promise of not only arresting the decline of the muscles of those affected by this inherited genetic disease, but perhaps, in ...

At Binghamton University, researchers were among the first to find ways to help patients with Duchenne muscular dystrophy ...

Muscular Dystrophy: Symptoms, Causes, Diagnosis and Treatment: By Anjali Srivastava Muscular dystrophy is a group of inherited conditions that cause gradual muscle weakness and loss of muscle mass. It ...

Gene therapy may have the potential to cure Duchenne muscular dystrophy, but early results from clinical trials have not been as promising as researchers hoped. Research is ongoing. Duchenne muscular ...

Physical therapy supports Duchenne muscular dystrophy (DMD) care by maintaining strength and flexibility, improving movement, and lowering the risk of contractures. A physical therapist also monitors ...

A drug from the same family licensed for use in patients with Duchenne muscular dystrophy and blood cancer could transform ...

Jason is a general assignment reporter, with particular focus on genetic medicine and rare disease. Confidential tips can be sent on Signal at JasonMast.77. An experimental gene therapy from Sarepta ...

Duchenne muscular dystrophy (DMD) is a neuromuscular disorder that results from mutations in the DMD gene. Gene therapies for DMD change genetic material in a person’s body to treat this condition.